Gene editing history will have a lot to say about 2021. That year, two in vivo CRISPR-based therapies showed promise in human trials. One of the therapeutics, from Intellia Therapeutics and Regeneron ...
Please provide your email address to receive an email when new articles are posted on . An experimental gene editing cell therapy for sickle cell disease has shown encouraging early results in a phase ...
A single injection of a novel CRISPR gene-editing treatment safely and efficiently removes SIV -- a virus related to the AIDS-causing agent HIV -- from the genomes of non-human primates, scientists ...
(Philadelphia, PA) – Genetic alterations that give rise to a rare, fatal disorder known as MOGS-CDG paradoxically also protect cells against infection by viruses. Now, scientists at the Lewis Katz ...
—Proprietary CRISPR-associated gene editing systems exhibited >95% efficiency in human primary cells and stem cells and ability to target key cancer-related genes while avoiding pre-existing immunity— ...
Researchers restored hearing in preclinical mouse models with a specific form of inherited deafness called DFNA50 caused by mutations in microRNA, by using a novel in vivo CRISPR genome editing ...
Researchers from the Department of Biomedical Engineering at UNIST and the Center for Genomic Integrity at the Institute for Basic Science (IBS) have announced an advance in cancer gene therapy. Their ...
Jennifer Doudna and Emmanuelle Charpentier were awarded the 2020 Nobel Prize in Chemistry for their pioneering work in gene editing. The gene editing technique Doudna and Charpentier developed is ...